Pompe Disease Treatment Genzyme
Sanofi genzyme online has.
Pompe disease treatment genzyme. This is an important day for the pompe community especially for those patients with late onset pompe disease in the united states who are awaiting. Pompe disease is a rare genetic disease. People with pompe disease do not have enough of a particular enzyme to break down glycogen in their muscle cells. Cambridge mass business wire genzyme corp.
Genz today announced that the results from its late onset treatment study lots have been published in. Glycogen storage disease type ii. Health canada approved myozyme for the treatment of pompe disease. Genzyme received broad approval in the european union.
Pompe disease is a lysosomal storage disorder lsd caused by a deficiency in acid a glucosidase gaa also called acid maltase. Its a difficult debilitating disease but. Brian pompe patient. Sanofi genzyme does not review or control the content of non sanofi genzyme websites.
Pompe disease news is strictly a news and information website about the disease. It does not provide medical advice diagnosis or treatment. This content is not. About pompe disease.
Die within the first year or two of life without treatment. To pompe disease newsletter.